Miller’s Miracle: In Motion
Phase One: Functional Study
This November, we traveled to NextGen at the University of Missouri to kick off the functional study that represents phase one of finding Miller her miracle. The study is using a sample of Miller’s skin to allow her cells to be studied in vitro. This will include modeling her disease, or identifying exactly what is going on in her cells as a result of her genetic mutation.
From here, we will be able to test which therapeutics will have the highest probability of helping correct what is going wrong. Once we know these results, we can move onto phase two: developing the therapeutic.
Phase Two: Making A Miracle
Once we have the learnings of the functional study, we can begin to develop the therapeutic. Whether that’s a personalized gene therapy, RNA-based therapy, gene editing, or funding a trial for drug repurposing, we’re looking at a multi-million dollar endeavor for this next phase. With phase one successfully fully funded, we are focusing on funding phase two now. Join us is helping make Miller’s Miracle possible.
